With promise to slow aging and cure some types of cancer, a new gene therapy presents cost and access hurdles for CT patients ...

Eli Lilly and Regeneron are leading the push to treat congenital deafness with gene therapies, seeking a piece of a potential ...

Karmanos 1st debut novel gene therapy offers a one-time treatment for adult hemophilia B, reducing the need for routine factor IX infusions.

The Barbara Ann Karmanos Cancer Institute in Detroit has become the first and only independent cancer center in the U.S. to ...

Global stockout halts access to Hemgenix gene therapy, delaying treatment for adults with hemophilia B amid manufacturing ...

Researchers plan to begin the first patient trial in 2027 thanks to promising preclinical results from a gene therapy ...

An expert involved in the first successful gene therapy trial for Huntington's Disease discusses the trial results and ...

A genetic variant carried by at least one-fifth of the population may do far more than raise the odds of developing Alzheimer ...

OCGN's gene-agnostic eye therapy aims to treat multiple retinal mutations, with key filings and pivotal data in 2026???2027 set to test its broad platform.

The last available hemophilia gene therapy is temporarily unavailable, according to CSL Behring.  | The company is working ...

He is the first person in the state to receive LYFGENIA, a one-time gene therapy designed to keep the red blood cells that ...

Hemgenix for hemophilia B is temporarily unavailable, says maker CSL Behring ...